Genetics Treating Genetic Diseases

Question 1

Levels at which you can treat single gene defects:

[…]

Answer 1

Levels at which you can treat single gene defects:

1. Gene level
   - organ transplant
   - gene therapy
   - ***mRNA level (remove the mRNA)
   *
2. Clinical phenotype
   - mRNA (degrade the mRNA)
   - protein (replace them, etc.)
   - metabolism (diet, removing substance, etc.)
   - treat symptoms
3. Family level
   - genetic counselling
4. Environment level

Organ transplant is a gene level intervention